Patients & families
In this section:
We are devoted to creating better lives for people living with chronic debilitating disease. We work with families and patient organisations to ensure our programmes deliver the best treatments and resources for gene therapy and genetic disease.
We are transforming our innovative gene technology into potentially life-changing treatments.
We are working to bring a potential first- and best-in-class gene therapy to patients with Gaucher disease Type 1.
The following organisations offer resources and information to help people affected by Gaucher disease